{
  "patent_number": "US 12734160",
  "country": "US",
  "title": "Treating Lysosomal Storage Disease Symptoms with Quinuclidine Compounds",
  "original_title": "Methods for treating symptoms and disorders associated with lysosomal storage diseases",
  "summary": "This patent describes methods for using specific quinuclidine compounds, sometimes with enzyme replacement therapy, to treat symptoms like pain and skin issues in patients with lysosomal storage diseases such as Fabry disease.",
  "what_it_does": "This patent describes ways to treat or prevent specific symptoms and disorders linked to lysosomal storage diseases. It focuses on using 'quinuclidine compounds of formula (I)' for this purpose. The treatment can optionally be combined with enzyme replacement therapy. Examples of symptoms it aims to treat include pain, like abdominal pain, and skin problems such as angiokeratoma. The methods are intended for patients with diseases like Fabry disease.",
  "what_it_does_not_cover": [
    "Does not cover treatments using compounds other than quinuclidine compounds of formula (I).",
    "Does not cover treatments for diseases that are not classified as lysosomal storage diseases.",
    "Does not cover treatments for symptoms unrelated to pain or dermatological disorders in these diseases.",
    "Does not cover treatments for lysosomal storage diseases that do not involve either quinuclidine compounds or enzyme replacement therapy."
  ],
  "filed": "2020-02-03",
  "granted": "2026-09-15",
  "expires": null,
  "status": "active",
  "holder": null,
  "holder_url": null,
  "inventors": [],
  "times_cited": 0,
  "tags": [
    "pharmaceutical",
    "biotech",
    "rare_diseases"
  ],
  "abstract": "This disclosure to methods for treating or preventing particular symptoms and disorders which are associated with lysosomal storage diseases using quinuclidine compounds of formula (I), optionally in combination with enzyme replacement therapy. This includes pain, such as abdominal pain, and dermatological disorders, such as angiokeratoma, in a patient having a disease such as Fabry disease. Also disclosed is a pharmaceutical composition comprising a quinuclidine compound for use in said methods.",
  "url": "https://patentbrief.org/patent/us/12734160/methods-for-treating-symptoms-and-disorders-associated-with-lysosomal-storage",
  "markdown_url": "https://patentbrief.org/patent/us/12734160/methods-for-treating-symptoms-and-disorders-associated-with-lysosomal-storage/md",
  "google_patents_url": "https://patents.google.com/patent/US12734160",
  "relatedPatents": []
}